Current partner codePEPTIDESDE
NCT01637272·Phase 2·INTERVENTIONAL

Phase II Study Evaluating Efficacy, Safety and Pharmacokinetics of Pasireotide in Patients With Dumping Syndrome

Status

Completed

Phase

Phase 2

Enrollment

43

Locations

17

Results

Posted

Publications

0

Study summary

What the protocol is testing.

multi-center, phase II study evaluating efficacy, safety and pharmacokinetics of pasireotide in patients with dumping syndrome

Full detailed description

43 adult patients with dumping syndrome received pasireotide s.c. during the dose escalation phase (3 months dose could be increased based on the presence of hypoglycemia during OGTT). After completing Month 3, patients were switched to pasireotide LAR for 3 months (up to Month 6). The core phase of the study was completed at the end of Month 6. Patients were allowed to enter the 6 month extension phase if they experienced benefit with pasireotide LAR treatment.

Interventions

Treatment arms and agents.

DRUG

SOM230

Pasireotide (SOM230) sc injection was provided as solution for injection in individual 1-point-cut 1 mL ampule, containing nominally 200 μg of pasireotide (as free base). Doses: 50, 100, 150 and 200 μg. Pasireotide im LAR depot injection was provided as micro particles powder in vials containing nominally 10, 20, 40 \& 60 mg of pasireotide (as free base) \& solvent for suspension for injection in ampules for the reconstitution of the LAR micro particles. Doses: 10, 20, 30, 40 or 60 mg

Timeline

From registration to results.

  1. First posted

    Jul 11, 2012

  2. Study start

    Jan 8, 2013

  3. Primary completion

    Aug 7, 2015

  4. Study completion

    Aug 7, 2015

  5. Results posted

    May 10, 2017

  6. Registry updated

    May 10, 2017

Outcomes

What the study measures.

Primary outcomes

Response Rate in Plasma Glucose Level

Time frame · at Month 3 (M3)

Response rate is defined as percentage of patients with no glucose values \< 60 mg/dL at 90,120, 150 and 180 min during the Oral Glucose Tolerance Test (OGTT) at the end of s.c. dose escalation phase

Secondary outcomes

Response Rate in Plasma Glucose Level

Time frame · at Month 6 (M6), Month 12 (M12)

Response rate is defined as percentage of patients with no glucose values \< 60 mg/dL at 90,120, 150 and 180 min during the Oral Glucose Tolerance Test (OGTT) at the end of 6 months (end of LAR/Core phase) and at the end of 12 months (extension phase)

Response Rate in Pulse Rate

Time frame · at baseline, M3, M6, M12

Pulse rate was defined as percentage of patients with change in pulse rate \>=10 bpm from pre-OGTT to 30 minutes post OGTT.

Response Rate in Hematocrit Levels

Time frame · M3, M6, M12

Percentage of patients with change in hematocrit \>= 3% from pre-OGTT to 30 minutes post OGTT.

Insulin Levels During OGTT

Time frame · M3, M6, M12

Absolute insulin levels at the end of M3, M6, M12

Glucagon Levels During OGTT

Time frame · M3, M6, M12

Absolute glucagon levels at the end of Months 3, 6 \& 12

Glucagon-like Peptide 1 (GLP-1) Levels During OGTT

Time frame · M3, M6, M12

Absolute Glucagon-like peptide 1 (GLP-1) levels at the end of at the end of Months 3, 6 and 12 at different time points.

Gastric Inhibitory Polypeptide (GIP) Levels at During OGTT

Time frame · M3, M6, M12

Absolute Gastric Inhibitory Polypeptide (GIP) levels at the end of Months 3, 6 and 12 at different time points.

Health-related Quality of Live (HRQoL) Short Form- 36 (SF-36) Score(s)

Time frame · M3, M6, M12

Absolute HRQoL SF-36 Scores at end of the Months 3, 6 and 12 from s.c. baseline. SF-36, a 36-Item Short Form Health Survey (SF-36) is a set of generic, coherent, and easily administered quality-of-life measures. These measures rely upon patient self-reporting. Items are scored so that a high score defines a more favorable health state. In addition, each item is scored on a 0 to 100 range so that the lowest and highest possible scores are 0 and 100, respectively.

Dumping Severity Score (DSS) at the End of Months 3, 6 and 8

Time frame · M3, M6, M8

Absolute Dumping Severity Score (DSS) scores at end of M3, M6 \& M8. At study start patients were assessed using DSS (older version of DSQ); however after the implementation of protocol amendment 2, all patients were expected to use DSQ. No results available for M12 as last patient that answered the DSS was at M8. DSS = disease-specific patient (Pt.) reported outcome (PRO) questionnaire uses a 4-point Likert scale (0, absent; 1, mild; 2, relevant; 3, severe; 4) to ask Pt. to evaluate intensity of early dumping symptoms (within 30 minutes (\<30 minutes) after food ingestion). The questionnaire also evaluates 65 late dumping symptoms (more than 1.5 hours (\>90 minutes) after food ingestion). Early \& late dumping score calculated by adding the scores of the respective questions. Cumulative dumping score is obtained by adding early \& late scores. DSS Range (min (absent) - max (severe)): Early dumping: 0-24; Late Dumping: 0-18; Cumulative: 0-42. Lower scores represent a better outcome.

Dumping Score Questionnaire (DSQ) at the End of Months 3, 6 and 12

Time frame · M3, M6, M12

Absolute Dumping Score Questionnaire (DSQ) scores at end of Months 3, 6 \& 12 from s.c. baseline. DSQ = disease-specific PRO scale. The questionnaire uses a 5-point Likert scale (0, none; 1, mild; 2, moderate; 3, severe; 4, very severe) to ask Pt. to evaluate intensity of 10 early dumping symptoms (within 30 minutes (\<30 minutes) after food ingestion). The questionnaire also evaluates 5 late dumping symptoms (more than 1.5 hours (\>90 minutes) after food ingestion). Early \& late dumping score calculated by adding the scores of respective questions. A cumulative dumping score is obtained by adding early \& late scores. At study start patients were assessed using DSS (older version of DSQ); however after the implementation of protocol amendment 2, all patients used DSQ. DSQ Range: (min (None) - max (Very severe)): Early dumping: 0-40; Late Dumping: 0-20; Cumulative: 0-60. Lower scores represent a better outcome.

Eligibility

Who can take part.

Minimum age
18 Years
Maximum age
Not reported
Sex
ALL
Healthy volunteers
No

Inclusion criteria:. * Male or female patients ≥ 18 years of age. * Post-gastric or esophageal bypass surgery, matching one of the criteria below: * Bariatric surgery: more than 6 months before signing the informed consent * Esophageal cancer surgery: were disease free at study entry * Gastric cancer surgery: were at stage 0 or I and were disease free at study entry * Patient with a documented diagnosis of Dumping Syndrome defined as having: * History of/or active symptoms associated with dumping syndrome (e.g. post-prandial tachycardia, bloating, diarrhea) and * Documented history of hypoglycemia based on either: * glucose \<50 mg/dL or 2.8 mmol/L on a sporadic or scheduled blood analysis -or * glucose value \<60 mg/dL or ≤ 3.3 mmol/L at 90, 120, 150 or 180 min during an OGTT * Patients had at least one glucose level \<60 mg/dL (or ≤ 3.3 mmol/L) at 90, 120, 150 or 180 min during the 3-hour OGTT at screening. * Patients with esophageal cancer with a negative computed tomography (CT) or Magnetic resonance imaging (MRI) scan (neck, thoracic, and upper abdominal) and albumin ≥ 3.5 g/dl at baseline. * Patients with gastric cancer with a negative CT or MRI scan (total abdomen). * Karnofsky Performance Status ≥ 60 (i.e. required occasional assistance, but was able to care for most of their personal needs) * Patients who received other therapies for dumping syndrome (such as acarbose, gama guar, pectin) must have stopped all treatments and had a wash out period prior to signing the informed consent (i.e. at least 2 weeks between last previous therapy and first dose of study medication in this study). * Patients who had provided signed written informed consent prior to study participation. Exclusion Criteria: * Bariatric patients who had lap band. * Patients with a current diagnosis of diabetes mellitus. * Patients who had failed treatment with somatostatin analogues for dumping syndrome in the past. * Patients who had been treated with somatostatin analogues in the past, must have had an appropriate interval between the last administration of somatostatin analogues treatment and the study drug as follows * Octreotide sc for ≥ 72 hours * Octreotide LAR for ≥ 56 days (8 weeks) * Lanreotide Autogel for ≥ 98 days (14 weeks) * Lanreotide SR ≥ 28 days (4 weeks) * Patients who were already treated with pasireotide. * Patients who had a known hypersensitivity to somatostatin analogues. * Patients who were receiving anti-cancer therapy (chemotherapy and/or radiotherapy). * Patients who had any severe and/or uncontrolled medical conditions or other conditions that could affect their participation in the study such as: * Patients with the presence of active or suspected acute or chronic uncontrolled infection or with a history of immunodeficiency, including a positive human immunodeficiency virus (HIV) test result (ELISA and Western blot). An HIV test was not required; however, previous medical history was reviewed. * Non-malignant medical illnesses that were uncontrolled or whose control may have been jeopardized by the treatment with this study treatment. * Life-threatening autoimmune and ischemic disorders. * Patients with the presence of active or suspected acute or chronic uncontrolled infection. Inadequate end organ function as defined by: * Inadequate bone marrow function: * White blood cells (WBC) \<2.5 x 109/L * Absolute neutrophil count \<1.5 x 109/L * Platelets \<100 x 109/L * Hemoglobin \<9 g/dL * International normalized ratio (INR) ≥ 1.3 * Serum creatinine \>2.0 mg/dL * Alkaline phosphatase (ALP) \>2.5 x upper limit of normal (ULN) * Serum total bilirubin \>1.5 x ULN * Alanine aminotransferase (ALT) and aspartate aminotransferase (AST) \>2 x ULN * History of liver disease, such as cirrhosis or chronic active hepatitis B and C. * Presence of Hepatitis B surface antigen (HbsAg) and/ or presence of Hepatitis C antibody test (anti-Hepatitis C Virus).

Study locations

17 registered sites.

Belgium · France · Germany · Netherlands · United States. Showing up to 24 locations stored in the fast local snapshot.

Ximed Center for Weight Management Ximed Research

La Jolla, California, United States

Stanford University Medical Center SC - SOM230X2203

Stanford, California, United States

Mayo Clinic - Rochester Mayo MN

Rochester, Minnesota, United States

Montefiore Medical Center CLCZ696B2320

The Bronx, New York, United States

Texas Tech University Health Science Center

El Paso, Texas, United States

Virginia Endocrinology Research SC

Chesapeake, Virginia, United States

Novartis Investigative Site

Bruges, Belgium, Belgium

Novartis Investigative Site

Brussels, Belgium

Novartis Investigative Site

Ghent, Belgium

Novartis Investigative Site

Leuven, Belgium

Novartis Investigative Site

Paris, France

Novartis Investigative Site

Pessac, France

Novartis Investigative Site

Pierre-Bénite, France

Novartis Investigative Site

Hamburg, Germany

Novartis Investigative Site

Würzburg, Germany

Novartis Investigative Site

Utrecht, Netherlands, Netherlands

Novartis Investigative Site

Groningen, Netherlands

Publications

Results and literature.

No PMID-linked publications were present in this registry snapshot.

Primary links

Continue at the source.

Related trials

More studies on Pasireotide.

Related PeptideStat pages

Put the record in context.

Research pages describe evidence. Vendor pages, where available, describe independently tracked research-product listings and are not clinical recommendations.